British-Finnish Alliance to Bring Gene Therapy to the Masses
Two European Bio-Tech companies are investigating the suitability of combining the two companies’ technology into one powerful gene therapy.
British-Finnish Alliance to Bring Gene Therapy to the Masses
Gene Therapy Halts a Fatal Brain Disease
CRISPR Restores Muscle Function in Mice
Rare genetic diseases can arise from unsuspecting carriers
Introducing 123Genetix --- A New Non-Profit Organization Planning to Use Predictive Computer Models
Preliminary Phase 2 Data from Spinal Muscular Atrophy Program Presented at CureSMA Conference
Parents of child with rare GM1 Lysosomal Storage Disease Lead Search for Treatment
NIH scientists find rare disease clues in cell’s recycling system
New Data Provide Beneficial Evidence of Soliris (eculizumab) in PNH Patients
Seattle Genetics announced promising results from its Phase 3 ECHELON-1 in Frontline Advanced Hodgki