British-Finnish Alliance to Bring Gene Therapy to the Masses
Two European Bio-Tech companies are investigating the suitability of combining the two companies’ technology into one powerful gene therapy.
top of page
Free (or almost free) Digital Marketing Resources
Search
GINA KOLATA, NY Times
- Oct 18, 2017
- 1 min
Gene Therapy Halts a Fatal Brain Disease
Patients with a genetic disease, adrenoleukodystrophy, or ALD, causing brain cell death were successfully treated with gene therapy.
6 views0 comments
Diana Kwon, The Scientist
- Sep 1, 2017
- 1 min
CRISPR Restores Muscle Function in Mice
Using CRISPR, researchers have successfully treated congenital muscular dystrophy type 1A (MDC1A), a rare disease that can lead to severe mu
2 views0 comments
Ben Locwin, Genetic Literacy Project
- Sep 1, 2017
- 1 min
Rare genetic diseases can arise from unsuspecting carriers
COMMAD is a syndrome which presents, ocular holes, dense bones, small eyes, large head, albinism, and deafness. A rare example of a disease
8 views0 comments
PRWEB
- Sep 1, 2017
- 1 min
Introducing 123Genetix --- A New Non-Profit Organization Planning to Use Predictive Computer Models
123Genetix (www.123genetix.com) is developing a big data/deep learning solution to assist researchers: Develop new hypotheses; Design and ru
11 views0 comments
Admin
- Sep 1, 2017
- 1 min
Preliminary Phase 2 Data from Spinal Muscular Atrophy Program Presented at CureSMA Conference
PTC Therapeutics (NASDAQ: PTCT) is a global biopharmaceutical company focused on the discovery, development, and commercialization of novel
2 views0 comments
ROSE CAHALAN, Alcalde
- Sep 1, 2017
- 1 min
Parents of child with rare GM1 Lysosomal Storage Disease Lead Search for Treatment
When the Bragg family learned their daughter, Clara had GM1, a rare Lysosomal Storage Disease they, like many parents with children with rar
5 views0 comments
Admin
- Aug 18, 2017
- 1 min
NIH scientists find rare disease clues in cell’s recycling system
Research carried out on a Niemann-Pick type C1 (NPC1) treatment can lead to a new generation of potential therapies for NPC1 and other simil
20 views0 comments
Mathew Shanley, www.raredr.com
- Jun 25, 2017
- 1 min
New Data Provide Beneficial Evidence of Soliris (eculizumab) in PNH Patients
Alexion Pharmaceuticals, Inc. presented new data displaying benefits of Soliris (eculizumab) treatment for patients with PNH, regardless of
6 views0 comments
Mathew Shanley, www.raredr.com
- Jun 25, 2017
- 1 min
Seattle Genetics announced promising results from its Phase 3 ECHELON-1 in Frontline Advanced Hodgki
Takeda and Seattle Genetics announced promising results from its Phase 3 ECHELON-1 Clinical Trial that evaluated Adcetris in Frontline Advan
19 views0 comments
bottom of page